PATIENT REGISTRY

Built and run by NGLY1 Families.

Help us find a cure for NGLY 1 Deficiency.

Your child’s genetic information and symptoms could aid researchers in new discoveries and accelerating the development of therapies for NGLY1 patients. With your help, the global team working to cure NGLY1 can learn and do more. Please help us on this quest. It only takes a few minutes to improve lives.

JOIN OUR COMMUNITY

Thank you! Your submission has been received!
Oops! Something went wrong while submitting the form.