Maria Grazia Roncarolo, MD, is a Professor of Pediatrics and Medicine at Stanford School of Medicine, Chief of the Division of Pediatric Stem Cell Transplantation and Regenerative Medicine, Co-Director of the Bass Center for Childhood Blood Disease and Co-Director of the Institute for Stem Cell Biology and Regenerative Medicine. Her efforts focus on the translation of scientific discoveries in genetic diseases and regenerative medicine into novel patient therapies, including treatments based on stem cells and gene therapy. Dr. Roncarolo was a key member of the first team to carry out stem cell transplants given before birth to treat these genetic diseases. Dr. Roncarolo has brought many basic-science discoveries from the bench to patients in the field. She holds eight patents, with six more pending, for methods used in novel cell and gene therapies.